Just Gene Therapy is a not for profit organisation established to raise funds for gene therapy for cystic fibrosis.

Cystic fibrosis

Cystic fibrosis (or CF) is a life-threatening inherited condition, which affects the lungs, the digestive system and other organs, by interfering with the correct formulation of mucus. As a result, a build up of thick, sticky mucus prevents these organs from working properly. 90% of the deaths which are caused by cystic fibrosis are from lung failure.


Gene therapy

Initially focusing on the lung, the cause of the vast majority of deaths in people with CF, gene therapy aims to introduce a correct copy of the CF gene into the appropriate cells of the person's lungs enabling them to work as they should.

 

 

 

Fluorescent microscope image of CF in cells

CFTR protein is shown in red at the surface of cells in this fluorescent microscope image.

© Just Gene Therapy 2012-14 | Just Gene Therapy is raising money on behalf of Imperial College, an exempt charity*.